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Off Topic on Adult (=regenerative) cell technology, but very much related i.e. pills and drugs of which we do not know if they work
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TOPIC: Will FDA approve gene therapy for blindness ?

Will FDA approve gene therapy for blindness ? 09 Oct 2017 22:36 #10216

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Will FDA approve gene therapy for blindness ? 10 Oct 2017 08:58 #10218

  • b767cpt
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Interesting Hedge, I wonder if the FDA will approve this, will the Cytori machine be used? From the earlier post that FAS put up on the Mayo Clinic trial, Mayo used the Cytori machine because they found it to produce the purest form of cells.

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Will FDA approve gene therapy for blindness ? 10 Oct 2017 09:12 #10220

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b7
This is gene therapy NOT stem cell therapy !
Also, note the response rate vs what Cytori often produces
While it wont fix every indication, gene therapy has the potential to help many gene based disorders.

Of course, I once thought stem cell therapy could also have a broad application...LOL
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Will FDA approve gene therapy for blindness ? 10 Oct 2017 09:24 #10222

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myownhedgefund wrote: b7


Of course, I once thought stem cell therapy could also have a broad application...LOL



It still may have a broader application than we all ever dreamed of!

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Will FDA approve gene therapy for blindness ? 10 Oct 2017 09:32 #10224

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***It still may have a broader application than we all ever dreamed of! ***

Not a chance, lets just be happy survival likely for at least a short period of time.

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Will FDA approve gene therapy for blindness ? 10 Oct 2017 09:50 #10226

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myownhedgefund wrote: ***It still may have a broader application than we all ever dreamed of! ***

Not a chance, lets just be happy survival likely for at least a short period of time.


I was not just referring to CYTX!

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Will FDA approve gene therapy for blindness ? 10 Oct 2017 10:59 #10227

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In my view which is shared by a lot of people- just not Big Pharma- genetic disorders account for- at most- 10% of recognized disorders. The rest is induced by lifestyle and metabolic issues.

The danger being that they are going to treat metabolic issues with gene therapy, which will be a disaster.

Anyway- everybody must have heard of CAR-T technology- the big thing that all of pharma is chasing now and which I have been following for 4-5 years now, but have not written about. (will not start that too) Novartis recently got the first approval in Europe for one of these things which received a lot of criticism because of the price tag.

Anyway- just as a taste and some background-



Wikipedia link on CAR-T - HERE

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Board moderator and Site-owner. I still regret the day I started analysing the prospects of MacroPore (now Cytori) back in 2004- a left-over from the tech-bubble at that time from the century change in my portfolio- and became addicted to Cytori´s fat cell technology. :cry:

Will FDA approve gene therapy for blindness ? 10 Oct 2017 11:53 #10228

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I like what the CRISPR tech may bring...although messing with DNA can be scary.


As far as lifestyle and health...certainly a factor...but reactions to the same bad habits can be quite different in individuals and thus finding what makes one more susceptible than another may be helped by such investigations in the future.

Anyway...it was OT and advancements in science I always find interesting

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Will FDA approve gene therapy for blindness ? 11 Oct 2017 12:15 #10233

  • Wall Street Titan
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Amazing technology, Hedge, and CRSPR is even more mind boggling. The idea that one can edit out a defective gene is amazing. Been watching EDIT, CRSP and NTLA but waiting for an entry point.

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